A systems pharmacology model for gene therapy in sickle cell disease.
Cpt: Pharmacometrics & Systems Pharmacology
Zheng, Bo B; Wille, Lucia L; Peppel, Karsten K; Hagen, David D; Matteson, Andrew A; Ahlers, Jeffrey J; Schaff, James J; Hua, Fei F; Yuraszeck, Theresa T; Cobbina, Enoch E; Apgar, Joshua F JF; Burke, John M JM; Roberts, John J; Das, Raibatak R
Spectrum of BRCA1/2 variants in 940 patients from Argentina including novel, deleterious and recurrent germline mutations: impact on healthcare and clinical practice.
Oncotarget
Solano, Angela Rosaria AR; Cardoso, Florencia Cecilia FC; Romano, Vanesa V; Perazzo, Florencia F; Bas, Carlos C; Recondo, Gonzalo G; Santillan, Francisco Bernardo FB; Gonzalez, Eduardo E; Abalo, Eduardo E; Viniegra, María M; Michel, José Davalos JD; Nuñez, Lina María LM; Noblia, Cristina Maria CM; Mc Lean, Ignacio I; Canton, Enrique Diaz ED; Chacon, Reinaldo Daniel RD; Cortese, Gustavo G; Varela, Eduardo Beccar EB; Greco, Martín M; Barrientos, María Laura ML; Avila, Silvia Adela SA; Vuotto, Hector Daniel HD; Lorusso, Antonio A; Podesta, Ernesto Jorge EJ; Mando, Oscar Gaspar OG