Publications:

Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper-IgM syndrome.

Embo Molecular Medicine

Vavassori, Valentina V; Mercuri, Elisabetta E; Marcovecchio, Genni E GE; Castiello, Maria C MC; Schiroli, Giulia G; Albano, Luisa L; Margulies, Carrie C; Buquicchio, Frank F; Fontana, Elena E; Beretta, Stefano S; Merelli, Ivan I; Cappelleri, Andrea A; Rancoita, Paola Mv PM; Lougaris, Vassilios V; Plebani, Alessandro A; Kanariou, Maria M; Lankester, Arjan A; Ferrua, Francesca F; Scanziani, Eugenio E; Cotta-Ramusino, Cecilia C; Villa, Anna A; Naldini, Luigi L; Genovese, Pietro P

Publication Date: 2021-03-05

Variant appearance in text: CD4: 334G>T

PubMed Link: 33475257

Variant Present in the following documents:

• Main text
• EMMM-13-e13545.pdf

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