Prime editing for functional repair in patient-derived disease models.
Nature Communications
Schene, Imre F IF; Joore, Indi P IP; Oka, Rurika R; Mokry, Michal M; van Vugt, Anke H M AHM; van Boxtel, Ruben R; van der Doef, Hubert P J HPJ; van der Laan, Luc J W LJW; Verstegen, Monique M A MMA; van Hasselt, Peter M PM; Nieuwenhuis, Edward E S EES; Fuchs, Sabine A SA