Duchenne muscular dystrophy hiPSC-derived myoblast drug screen identifies compounds that ameliorate disease in mdx mice.
Jci Insight
Sun, Congshan C; Choi, In Young IY; Rovira Gonzalez, Yazmin I YI; Andersen, Peter P; Talbot, C Conover CC; Iyer, Shama R SR; Lovering, Richard M RM; Wagner, Kathryn R KR; Lee, Gabsang G