Effective, safe, and sustained correction of murine XLA using a UCOE-BTK promoter-based lentiviral vector.
Molecular Therapy. Methods & Clinical Development
Seymour, Brenda J BJ; Singh, Swati S; Certo, Hannah M HM; Sommer, Karen K; Sather, Blythe D BD; Khim, Socheath S; Clough, Courtnee C; Hale, Malika M; Pangallo, Joseph J; Ryu, Byoung Y BY; Khan, Iram F IF; Adair, Jennifer E JE; Rawlings, David J DJ