Restoring Ureagenesis in Hepatocytes by CRISPR/Cas9-mediated Genomic Addition to Arginase-deficient Induced Pluripotent Stem Cells.
Molecular Therapy. Nucleic Acids
Lee, Patrick C PC; Truong, Brian B; Vega-Crespo, Agustin A; Gilmore, W Blake WB; Hermann, Kip K; Angarita, Stephanie Ak SA; Tang, Jonathan K JK; Chang, Katherine M KM; Wininger, Austin E AE; Lam, Alex K AK; Schoenberg, Benjamen E BE; Cederbaum, Stephen D SD; Pyle, April D AD; Byrne, James A JA; Lipshutz, Gerald S GS