Generation of a High Number of Healthy Erythroid Cells from Gene-Edited Pyruvate Kinase Deficiency Patient-Specific Induced Pluripotent Stem Cells.
Stem Cell Reports
Garate, Zita Z; Quintana-Bustamante, Oscar O; Crane, Ana M AM; Olivier, Emmanuel E; Poirot, Laurent L; Galetto, Roman R; Kosinski, Penelope P; Hill, Collin C; Kung, Charles C; Agirre, Xabi X; Orman, Israel I; Cerrato, Laura L; Alberquilla, Omaira O; Rodriguez-Fornes, Fatima F; Fusaki, Noemi N; Garcia-Sanchez, Felix F; Maia, Tabita M TM; Ribeiro, Maria L ML; Sevilla, Julian J; Prosper, Felipe F; Jin, Shengfang S; Mountford, Joanne J; Guenechea, Guillermo G; Gouble, Agnes A; Bueren, Juan A JA; Davis, Brian R BR; Segovia, Jose C JC
Genome-wide identification of microRNA expression quantitative trait loci.
Nature Communications
Huan, Tianxiao T; Rong, Jian J; Liu, Chunyu C; Zhang, Xiaoling X; Tanriverdi, Kahraman K; Joehanes, Roby R; Chen, Brian H BH; Murabito, Joanne M JM; Yao, Chen C; Courchesne, Paul P; Munson, Peter J PJ; O'Donnell, Christopher J CJ; Cox, Nancy N; Johnson, Andrew D AD; Larson, Martin G MG; Levy, Daniel D; Freedman, Jane E JE