Time to treatment benefit for adult patients with Fabry disease receiving agalsidase β: data from the Fabry Registry.
Journal Of Medical Genetics
Ortiz, Alberto A; Abiose, Ademola A; Bichet, Daniel G DG; Cabrera, Gustavo G; Charrow, Joel J; Germain, Dominique P DP; Hopkin, Robert J RJ; Jovanovic, Ana A; Linhart, Aleš A; Maruti, Sonia S SS; Mauer, Michael M; Oliveira, João P JP; Patel, Manesh R MR; Politei, Juan J; Waldek, Stephen S; Wanner, Christoph C; Yoo, Han-Wook HW; Warnock, David G DG