Patient-Specific iPSC-Derived Endothelial Cells Provide Long-Term Phenotypic Correction of Hemophilia A.
Stem Cell Reports
Olgasi, Cristina C; Talmon, Maria M; Merlin, Simone S; Cucci, Alessia A; Richaud-Patin, Yvonne Y; Ranaldo, Gabriella G; Colangelo, Donato D; Di Scipio, Federica F; Berta, Giovanni N GN; Borsotti, Chiara C; Valeri, Federica F; Faraldi, Francesco F; Prat, Maria M; Messina, Maria M; Schinco, Piercarla P; Lombardo, Angelo A; Raya, Angel A; Follenzi, Antonia A